Category | Funding IC | Project Number | Sub Project # | Project Title | PI Name | Org Name | State / Country | Amount |
Cooley's Anemia
|
NHLBI
|
5K23HL076468-04
|
|
Zinc and Bone Metabolism in Thalassemia
|
FUNG, ELLEN
|
CHILDREN'S HOSPITAL & RES CTR AT OAKLAND
|
CA
|
$127,369
|
Cooley's Anemia
|
NIDDK
|
5R37DK049108-14
|
|
Iron Chelators Predicated on Desferrithiocin
|
BERGERON, RAYMOND
|
UNIVERSITY OF FLORIDA
|
FL
|
$562,313
|
Cooley's Anemia
|
NHLBI
|
5R01HL087427-02
|
|
The Role of Alpha Hemoglobin Stabilizing Protein in Human Beta Thalassemia
|
WEISS, MITCHELL
|
CHILDREN'S HOSPITAL OF PHILADELPHIA
|
PA
|
$411,979
|
Cooley's Anemia
|
NHLBI
|
5R01HL024415-29
|
|
Beta-globin Transcriptional Regulation
|
ENGEL, JAMES
|
UNIVERSITY OF MICHIGAN AT ANN ARBOR
|
MI
|
$408,040
|
Cooley's Anemia
|
NHLBI
|
1R01HL090921-01
|
|
Cell selection strategies for the gene therapy of the beta-hemoglobinopathies
|
LEBOULCH, PHILIPPE
|
BRIGHAM AND WOMEN'S HOSPITAL
|
MA
|
$424,226
|
Cooley's Anemia
|
NIDDK
|
2R01DK053298-11
|
|
A Comparative Approach To Globin Regulation/Thalassemia
|
ZON, LEONARD
|
CHILDREN'S HOSPITAL BOSTON
|
MA
|
$359,125
|
Cooley's Anemia
|
NHLBI
|
1K08HL088260-01A1
|
|
REGULATORY T CELLS, MIXED CHIMERISM: A NOVEL TRANSPLANT STRATEGY FOR THALASSEMIAS
|
PILLAI, ASHA
|
STANFORD UNIVERSITY
|
CA
|
$130,599
|
Cooley's Anemia
|
NIDDK
|
5K01DK063992-05
|
|
Gene therapy for Cooley's anemia in a new mouse model
|
RIVELLA, STEFANO
|
WEILL MEDICAL COLLEGE OF CORNELL UNIV
|
NY
|
$129,133
|
Cooley's Anemia
|
NIDDK
|
5R37DK044746-17
|
|
Function of human & mouse Beta-globin locus control regions
|
GROUDINE, MARK
|
FRED HUTCHINSON CANCER RESEARCH CENTER
|
WA
|
$635,372
|
Cooley's Anemia
|
NIDDK
|
2R01DK045365-16A1
|
|
Globin Gene Switching: Molecular Control
|
STAMATOYANNOPOULOS, GEORGE
|
UNIVERSITY OF WASHINGTON
|
WA
|
$370,277
|
Cooley's Anemia
|
NHLBI
|
5R01HL082754-02
|
|
Nucleolin-mediated stabilization of human B-globin mRNA
|
RUSSELL, J
|
UNIVERSITY OF PENNSYLVANIA
|
PA
|
$393,750
|
Cooley's Anemia
|
NHLBI
|
2R44HL068354-02A2
|
|
Optimization of Iron Chelator Delivery System
|
GWATHMEY, JUDITH
|
GWATHMEY, INC.
|
MA
|
$2,425,024
|
Cooley's Anemia
|
NIDDK
|
5R01DK052356-13
|
|
Structure and Function of the Human Beta-Globin Locus Control Region
|
BUNGERT, JORG
|
UNIVERSITY OF FLORIDA
|
FL
|
$250,474
|
Cooley's Anemia
|
NHLBI
|
5R01HL057619-11
|
|
Mouse Model of Sickle Cell Disease and Genetic Therapies
|
TOWNES, TIM
|
UNIVERSITY OF ALABAMA AT BIRMINGHAM
|
AL
|
$426,051
|
Cooley's Anemia
|
NHLBI
|
5R01HL077765-03
|
|
RBC Ion Transporters as Hemoglobinopathy Risk Modifiers
|
ALPER, SETH
|
BETH ISRAEL DEACONESS MEDICAL CENTER
|
MA
|
$390,245
|
Cooley's Anemia
|
NIDDK
|
5R01DK029902-27
|
|
Globin Gene Expression during Erythroid Differentiation
|
GINDER, GORDON
|
VIRGINIA COMMONWEALTH UNIVERSITY
|
VA
|
$299,341
|
Cooley's Anemia
|
NIDDK
|
5R01DK074694-02
|
|
Role of KLF2 in erythropoiesis and globin expression
|
LLOYD, JOYCE
|
VIRGINIA COMMONWEALTH UNIVERSITY
|
VA
|
$299,341
|
Cooley's Anemia
|
NHLBI
|
2U54HL070590-06
|
0006
|
Hematopoietic stem cell gene therapy for sickle cell disease
|
PERSONS, DEREK
|
ST. JUDE CHILDREN'S RESEARCH HOSPITAL
|
TN
|
$548,197
|
Cooley's Anemia
|
NIDDK
|
2R01DK061692-06A1
|
|
Molecular and Biological Activities of Alpha Hemoglobin Stabilizing Protein
|
WEISS, MITCHELL
|
CHILDREN'S HOSPITAL OF PHILADELPHIA
|
PA
|
$361,682
|
Cooley's Anemia
|
NHLBI
|
2R01HL073439-05A2
|
|
Molecular Mechanism of Human Gamma-Globin Gene Silencing
|
LI, QILIANG
|
UNIVERSITY OF WASHINGTON
|
WA
|
$390,000
|
Cooley's Anemia
|
NHLBI
|
5K08HL088231-03
|
|
Study of bone disease in Thalassemia
|
VOGIATZI, MARIA
|
WEILL MEDICAL COLLEGE OF CORNELL UNIV
|
NY
|
$126,090
|
Cooley's Anemia
|
NIDDK
|
1R21DK078442-01A1
|
|
HRI/elF2aP Signaling Pathway as Potential Pharmaceutical Targets for Thalassemia
|
CHEN, JANE-JANE
|
MASSACHUSETTS INSTITUTE OF TECHNOLOGY
|
MA
|
$252,000
|
Cooley's Anemia
|
NHLBI
|
5U01HL065232-09
|
|
Thalassemia Clinical Research Network
|
KWIATKOWSKI, JANET
|
CHILDREN'S HOSPITAL OF PHILADELPHIA
|
PA
|
$1
|
Cooley's Anemia
|
NHLBI
|
5U01HL065239-09
|
|
Thalassemia Clinical Research Network
|
VICHINSKY, ELLIOTT
|
CHILDREN'S HOSPITAL & RES CTR AT OAKLAND
|
CA
|
$215,789
|
Cooley's Anemia
|
NHLBI
|
5U01HL065260-09
|
|
Thalassemia Clinical Research Network
|
NEUFELD, ELLIS
|
CHILDREN'S HOSPITAL BOSTON
|
MA
|
$1
|
Cooley's Anemia
|
NHLBI
|
5U01HL065244-09
|
|
Thalassemia Clinical Research Network
|
GIARDINA, PATRICIA
|
WEILL MEDICAL COLLEGE OF CORNELL UNIV
|
NY
|
$105,340
|
Cooley's Anemia
|
NHLBI
|
5K23HL077409-04
|
|
Pulmonary Hypertension in Thalassemia
|
SINGER, SYLVIA
|
CHILDREN'S HOSPITAL & RES CTR AT OAKLAND
|
CA
|
$144,531
|
Cooley's Anemia
|
NHLBI
|
5K01HL080954-04
|
|
Transgenic Analysis of Beta Globin Switching
|
CAMPBELL, ANDREW
|
UNIVERSITY OF MICHIGAN AT ANN ARBOR
|
MI
|
$150,120
|
Cooley's Anemia
|
NHLBI
|
5U01HL065238-09
|
|
Thalassemia Clinic Research Network
|
MCKINLAY, SONJA
|
NEW ENGLAND RESEARCH INSTITUTES, INC.
|
MA
|
$2,097,860
|
Cooley's Anemia
|
NIDDK
|
5R21DK075731-02
|
|
Chromatin loops at the beta globin locus
|
BLOBEL, GERD
|
CHILDREN'S HOSPITAL OF PHILADELPHIA
|
PA
|
$201,513
|
Cooley's Anemia
|
NIDDK
|
5R21DK071575-02
|
|
The role of hepcidin in beta-thalassemia
|
RIVELLA, STEFANO
|
WEILL MEDICAL COLLEGE OF CORNELL UNIV
|
NY
|
$246,960
|
Cooley's Anemia
|
NHLBI
|
5R37HL065449-09
|
|
Alpha-globin expression: post transcriptional mechanisms
|
LIEBHABER, STEPHEN
|
UNIVERSITY OF PENNSYLVANIA
|
PA
|
$338,242
|
Cooley's Anemia
|
NIDDK
|
5R01DK069646-04
|
|
Genetic Modulation of HbF in Beta Thalassemia
|
CHUI, DAVID
|
BOSTON UNIVERSITY MEDICAL CAMPUS
|
MA
|
$567,690
|
Cooley's Anemia
|
NHLBI
|
5R01HL082655-02
|
|
Targeted Correction of the Human Beta-globin Gene
|
GLAZER, PETER
|
YALE UNIVERSITY
|
CT
|
$413,345
|
Cooley's Anemia
|
NIDDK
|
1R01DK081290-01A1
|
|
Transactivation of Fetal Hemoglobin
|
PETERSON, KENNETH
|
UNIVERSITY OF KANSAS MEDICAL CENTER
|
KS
|
$318,750
|
Cooley's Anemia
|
NHLBI
|
2R01HL069234-06A2
|
|
Gamma Globin Induction: Molecular and Cell-Based Strategies
|
PACE, BETTY
|
UNIVERSITY OF TEXAS DALLAS
|
TX
|
$400,685
|
Cooley's Anemia
|
NHLBI
|
5P01HL032262-27
|
0014
|
Genetic Approaches to Hemoglobin Switching
|
ORKIN, STUART
|
CHILDREN'S HOSPITAL BOSTON
|
MA
|
$333,355
|
Cooley's Anemia
|
NHLBI
|
5P01HL032262-27
|
0016
|
Role of zfp148 (ZBP-89) in Erythroid Development
|
CANTOR, ALAN
|
CHILDREN'S HOSPITAL BOSTON
|
MA
|
$200,007
|
Cooley's Anemia
|
OD
|
2R56HL067336-05A2
|
|
Locus-linked Regulatory Motifs of Globin Gene Switching
|
PETERSON, KENNETH
|
UNIVERSITY OF KANSAS MEDICAL CENTER
|
KS
|
$367,500
|
Cooley's Anemia
|
NHGRI
|
3R01HL077765-03S1
|
|
RBC Ion Transporters as Hemoglobinopathy Risk Modifiers
|
ALPER, SETH
|
BETH ISRAEL DEACONESS MEDICAL CENTER
|
MA
|
$7,407
|
Cooley's Anemia
|
NHLBI
|
3R01HL077765-03S1
|
|
RBC Ion Transporters as Hemoglobinopathy Risk Modifiers
|
ALPER, SETH
|
BETH ISRAEL DEACONESS MEDICAL CENTER
|
MA
|
$14,906
|
Cooley's Anemia
|
NHLBI
|
5U01HL065233-09
|
0001
|
PROSPECTIVE COMPARISON OF TWO REGIMENS OF DEFEROXAMINE
|
OLIVIERI, NANCY
|
HOSPITAL FOR SICK CHLDRN (TORONTO)
|
CANADA
|
$90,745
|
Cooley's Anemia
|
NHLBI
|
5U01HL065233-09
|
0002
|
AUGMENTATION OF FETAL HEMOGLOBIN IN THALASSEMIA
|
OLIVIERI, NANCY
|
HOSPITAL FOR SICK CHLDRN (TORONTO)
|
CANADA
|
$90,746
|
Cooley's Anemia
|
NHLBI
|
5P01HL036444-28
|
0014
|
Allogeneic Hematopoietic Cell Transplantation for Nonmalignant Disorders
|
STORB, RAINER
|
FRED HUTCHINSON CANCER RESEARCH CENTER
|
WA
|
$154,231
|
Cooley's Anemia
|
NHLBI
|
5P01HL053749-15
|
0011
|
Factors modulating gamma globin gene expression
|
CUNNINGHAM, JOHN
|
ST. JUDE CHILDREN'S RESEARCH HOSPITAL
|
TN
|
$400,762
|
Cooley's Anemia
|
NHLBI
|
5P01HL053750-15
|
0011
|
Safe and Efficient Lentiviral Gene Transfer into HSC
|
NALDINI, LUIGI
|
UNIVERSITY OF WASHINGTON
|
WA
|
$251,299
|
Cooley's Anemia
|
NCRR
|
2M01RR000043-48
|
6854
|
EARLY DETECTION OF IRON CARDIOMYOPATHY IN THALESSEMIA
|
WOOD, JOHN
|
UNIVERSITY OF SOUTHERN CALIFORNIA
|
CA
|
$91,331
|
Cooley's Anemia
|
NIAID
|
1Z01AI001000-02
|
|
Malaria Pathogenesis and Human Immunity
|
FAIRHURST, RICK
|
NIH
|
|
$144,940
|
Cooley's Anemia
|
NIAID
|
1Z01AI001066-01
|
|
International Research in Cambodia: Malaria Research
|
WELLEMS, THOMAS
|
NIH
|
|
$728,988
|
Cooley's Anemia
|
NIDDK
|
1Z01DK015612-02
|
|
Developmental regulation of mammalian genes by transcription activators
|
DEAN, ANN
|
NIH
|
|
$429,258
|
Cooley's Anemia
|
NIDDK
|
1Z01DK025016-34
|
|
Pharmacological Control Of Human Hemoglobin Gene Expression
|
SCHECHTER, ALAN
|
NIH
|
|
$131,459
|
Cooley's Anemia
|
NIDDK
|
1Z01DK025021-33
|
|
Globin Gene Expression And Treatment Of Sickle Cell Anemia
|
NOGUCHI, CONSTANCE
|
NIH
|
|
$263,223
|
Cooley's Anemia
|
NIDDK
|
1Z01DK025100-02
|
|
Diagnosis and Treatment of Iron Overload.
|
MILLER, JEFFERY
|
NIH
|
|
$374,632
|
Cooley's Anemia
|
NIDDK
|
1Z01DK025101-02
|
|
Regulation of Fetal Hemoglobin Production in Humans.
|
MILLER, JEFFERY
|
NIH
|
|
$374,632
|
Cooley's Anemia
|
NHGRI
|
1Z01HG200340-02
|
|
Gene Therapy for Hemoglobin Disorders
|
BODINE, DAVID
|
NIH
|
|
$432,429
|
Cooley's Anemia
|
NHLBI
|
1Z01HL005802-03
|
|
Synergy of Hydroxyurea and Erythropoietin on Fetal Hemoglobin in SCD
|
GLADWIN, MARK
|
NIH
|
|
$635,991
|
Cooley's Anemia
|
NIDDK
|
1Z01HL006003-01
|
|
Effects Of Thalidomide and Stem Cell Factor On Fetal Hemoglobin Synthesis
|
RODGERS, GRIFFIN
|
NIH
|
|
$274,625
|
Cooley's Anemia
|
NIDDK
|
1Z01HL006006-01
|
|
Cloning And Characterization Of A Hydroxyurea-inducible Gene
|
RODGERS, GRIFFIN
|
NIH
|
|
$274,625
|
Cooley's Anemia
|
NIDDK
|
1Z01HL006007-01
|
|
Nonmyeloablative allogeneic PBSC in globin disorders
|
TISDALE, JOHN
|
NIH
|
|
$384,475
|
Cooley's Anemia
|
NIDDK
|
1Z01HL006008-01
|
|
A preclinical large animal model for globin gene transfer
|
TISDALE, JOHN
|
NIH
|
|
$329,550
|